Unclassified · Medical Literature

Cardiotoxic Effects and Microdystrophin Expression after Gene Therapy for DMD

Authors

Benjamin J. Samelson-JonesCristina Martos-RusCarolyn M. YrigollenLuis TecedorJuliana C. SmallSusan E. MatesanzConnor T. WatsonAndrew R. Vanden HeuvelSean CarrigSabrina W. YumJohn F. BrandsemaKimberly LinCarol Wittlieb-WeberAngela N. ViaenePierre P. RussoChildren’s Hospital of Philadelphia, PhiladelphiaSara PartingtonUniversity of Pennsylvania, PhiladelphiaKatie HuynhTiffany SeneviratneChildren’s Hospital of Philadelphia, PhiladelphiaSilvia Juarez RojasBhavya S. DoshiEmory University School of Medicine, AtlantaPerry ShiehDavid Geffen School of Medicine, University of California, Los Angeles, Los AngelesKevin M. FlaniganEmma FrairStefan NicolauNationwide Children’s Hospital, Columbus, OHMichael W. LawlorDiverge Translational Science Laboratory, MilwaukeeJulie M. CrudeleUniversity of Washington School of Medicine, SeattleBeverly L. DavidsonLindsey A. GeorgeChildren’s Hospital of Philadelphia, Philadelphia

Journal

New England Journal of Medicine

Publication date

2026-07-22

Source

rss_nejm

Original record ID

210131

Summary status

error

Analysis status

error

Original last updated

2026-08-10T06:47:18.000Z

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